{"id":13191,"date":"2024-10-21T09:01:32","date_gmt":"2024-10-21T08:01:32","guid":{"rendered":"https:\/\/romevisionclinic.com\/?p=13191"},"modified":"2024-10-21T09:07:19","modified_gmt":"2024-10-21T08:07:19","slug":"maculopatia-essudativa-una-terapia-genica-potrebbe-curarla-con-una-sola-iniezione","status":"publish","type":"post","link":"https:\/\/romevisionclinic.com\/it\/maculopatia-essudativa-una-terapia-genica-potrebbe-curarla-con-una-sola-iniezione\/","title":{"rendered":"Maculopatia essudativa: una terapia genica potrebbe curarla con una sola iniezione"},"content":{"rendered":"\t\t<div data-elementor-type=\"wp-post\" data-elementor-id=\"13191\" class=\"elementor elementor-13191\">\n\t\t\t\t\t\t<section class=\"elementor-section elementor-top-section elementor-element elementor-element-9dae3d6 elementor-section-boxed elementor-section-height-default elementor-section-height-default\" data-id=\"9dae3d6\" data-element_type=\"section\" 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.elementor-widget-empty-icon,.e-con>.elementor-widget-spacer.elementor-widget-empty .elementor-widget-empty-icon{position:absolute;top:0;bottom:0;left:0;right:0;margin:auto;padding:0;width:22px;height:22px}<\/style>\t\t<div class=\"elementor-spacer\">\n\t\t\t<div class=\"elementor-spacer-inner\"><\/div>\n\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<section class=\"elementor-section elementor-inner-section elementor-element elementor-element-4e8eca3 elementor-section-boxed elementor-section-height-default elementor-section-height-default\" data-id=\"4e8eca3\" data-element_type=\"section\">\n\t\t\t\t\t\t<div class=\"elementor-container elementor-column-gap-default\">\n\t\t\t\t\t<div class=\"elementor-column elementor-col-50 elementor-inner-column elementor-element elementor-element-0135f02\" data-id=\"0135f02\" data-element_type=\"column\">\n\t\t\t<div class=\"elementor-widget-wrap elementor-element-populated\">\n\t\t\t\t\t\t<div class=\"elementor-element elementor-element-83c1d8c elementor-drop-cap-yes elementor-drop-cap-view-default elementor-widget elementor-widget-text-editor\" data-id=\"83c1d8c\" data-element_type=\"widget\" data-settings=\"{&quot;drop_cap&quot;:&quot;yes&quot;}\" data-widget_type=\"text-editor.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t<style>\/*! elementor - v3.20.0 - 26-03-2024 *\/\n.elementor-widget-text-editor.elementor-drop-cap-view-stacked .elementor-drop-cap{background-color:#69727d;color:#fff}.elementor-widget-text-editor.elementor-drop-cap-view-framed .elementor-drop-cap{color:#69727d;border:3px solid;background-color:transparent}.elementor-widget-text-editor:not(.elementor-drop-cap-view-default) .elementor-drop-cap{margin-top:8px}.elementor-widget-text-editor:not(.elementor-drop-cap-view-default) .elementor-drop-cap-letter{width:1em;height:1em}.elementor-widget-text-editor .elementor-drop-cap{float:left;text-align:center;line-height:1;font-size:50px}.elementor-widget-text-editor .elementor-drop-cap-letter{display:inline-block}<\/style>\t\t\t\t<p>Trattare la <strong>maculopatia essudativa<\/strong> con <strong>una sola iniezione intravitreale<\/strong> \u00e8 l\u2019<strong>obiettivo a cui stanno lavorando da diversi anni alcuni gruppi di ricerca internazionali<\/strong>.<\/p>\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-1c60f5e elementor-widget elementor-widget-text-editor\" data-id=\"1c60f5e\" data-element_type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t\t\t\t\t<p>Oggigiorno i pazienti affetti da maculopatia essudativa devono aderire a una <strong>terapia iniettiva<\/strong> a base di <strong>anti-VEGF<\/strong>, che prevede di iniettare direttamente all\u2019interno dell\u2019occhio, mediante <strong>iniezione intravitreale<\/strong>, un farmaco in grado di contrastare il <strong>VEGF<\/strong>, il <strong>principale responsabile della proliferazione incontrollata dei vasi sanguigni patologici<\/strong> che causano il <strong>danno retinico e visivo<\/strong> tipico della patologia.<\/p>\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-133afe0 elementor-widget elementor-widget-text-editor\" data-id=\"133afe0\" data-element_type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t\t\t\t\t<p>La terapia iniettiva con anti-VEGF presenta un <strong>elevato grado di sicurezza ed efficacia<\/strong>, tuttavia il dover ripetere le iniezioni a intervalli di tempo anche piuttosto frequenti (in media dalle 4 alle 8 settimane) comporta <strong>alti livelli di ansia e stress per i pazienti<\/strong>, oltre che <strong>un\u2019ingente spesa per il sistema sanitario<\/strong>.<\/p>\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t<\/div>\n\t\t\t\t<div class=\"elementor-column elementor-col-50 elementor-inner-column elementor-element elementor-element-bd56db1\" data-id=\"bd56db1\" data-element_type=\"column\">\n\t\t\t<div class=\"elementor-widget-wrap elementor-element-populated\">\n\t\t\t\t\t\t<div class=\"elementor-element elementor-element-ff2a286 elementor-widget elementor-widget-image\" data-id=\"ff2a286\" data-element_type=\"widget\" data-widget_type=\"image.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t<style>\/*! elementor - v3.20.0 - 26-03-2024 *\/\n.elementor-widget-image{text-align:center}.elementor-widget-image a{display:inline-block}.elementor-widget-image a img[src$=\".svg\"]{width:48px}.elementor-widget-image img{vertical-align:middle;display:inline-block}<\/style>\t\t\t\t\t\t\t\t\t\t<img fetchpriority=\"high\" decoding=\"async\" width=\"724\" height=\"483\" 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d=\"M41.9,19.3c0,0,1.2-0.3,2.9-0.1c1.7,0.2,5.8,0.9,8.2,0.7c4.2-0.4,7.4-2.7,7-2.6\tc-0.4,0-4.3,2.2-8.6,1.9c-1.8-0.1-5.1-0.5-6.7-0.4S41.9,19.3,41.9,19.3z\"\/>\n\t<path class=\"elementor-shape-fill\" d=\"M75.5,12.6c0.2,0.1,2-0.8,4.3-1.1c2.3-0.2,2.1-0.3,2.1-0.5c0-0.1-1.8-0.4-3.4,0\tC76.9,11.5,75.3,12.5,75.5,12.6z\"\/>\n\t<path class=\"elementor-shape-fill\" d=\"M15.6,13.2c0-0.1,4.3,0,6.7,0.5c2.4,0.5,5,1.9,5,2c0,0.1-2.7-0.8-5.1-1.4\tC19.9,13.7,15.7,13.3,15.6,13.2z\"\/>\n<\/svg>\t\t<\/div>\n\t\t\t\t\t<div class=\"elementor-container elementor-column-gap-default\">\n\t\t\t\t\t<div class=\"elementor-column elementor-col-100 elementor-top-column elementor-element elementor-element-29564d4\" data-id=\"29564d4\" data-element_type=\"column\">\n\t\t\t<div class=\"elementor-widget-wrap elementor-element-populated\">\n\t\t\t\t\t\t<div class=\"elementor-element elementor-element-77df92b elementor-widget elementor-widget-text-editor\" data-id=\"77df92b\" data-element_type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t\t\t\t\t<p>Oculisti e pazienti conoscono bene il peso psicologico ed economico della terapia a base di anti-VEGF e dati recenti hanno fatto emergere che <strong>pi\u00f9 del 40% dei pazienti interrompe il trattamento iniettivo dopo i primi 3 anni, con gravi conseguenze sul loro visus<\/strong>.<\/p><p>La ricerca di nuove strategie terapeutiche in grado di contrastare l\u2019effetto patologico della maculopatia essudativa in modo definitivo \u2013 o almeno per periodi molto lunghi \u2013 si \u00e8 avvalsa delle <strong>tecniche di terapia genica<\/strong>, che prevedono di introdurre nelle cellule della retina del paziente un<strong> DNA terapeutico<\/strong> in grado di fornire tutte le <strong>istruzioni necessarie a produrre il farmaco anti-VEGF direttamente <em>in loco<\/em><\/strong><em>.<\/em><\/p><p>L\u2019introduzione del DNA terapeutico nelle cellule retiniche del paziente avverrebbe in u<strong>n\u2019unica somministrazione mediante iniezione intravitreale<\/strong> e <strong>la produzione di anti-VEGF all\u2019interno dell\u2019occhio eviterebbe di dover ricorrere alle iniezioni intravitreali di anti-VEGF o al limite di dovervi ricorrere con una frequenza estremamente limitata.<\/strong><\/p><p>La terapia genica pi\u00f9 promettente per la cura definitiva della maculopatia essudativa si chiama <strong>Ixo-vec<\/strong> (<strong>Ixoberogene Soroparvovec<\/strong>) ed \u00e8 stata creata dalla <strong>Adverum Biotechnologies<\/strong>. Una volta iniettato, Ixo-vec dovrebbe garantire un <strong>effetto terapeutico efficace e duraturo in assenza di eventi avversi significativi<\/strong>.<\/p><p>Per questa nuova terapia genica sono stati eseguiti uno <strong>studio clinico di Fase I<\/strong>, denominato <strong>OPTIC<\/strong>, e uno <strong>studio clinico di Fase II<\/strong>, <strong>denominato LUNA<\/strong>, tutt\u2019ora in corso.<\/p><p>I pazienti che hanno partecipato allo studio OPTIC sono rimasti quasi tutti indipendenti dalla terapia iniettiva per oltre 3 anni, un risultato estremamente incoraggiante. Il successivo studio LUNA mira a verificare se \u00e8 possibile <strong>ottenere risultati migliori trattando i pazienti con dosi di farmaco pi\u00f9 basse combinate con regimi profilattici potenziati<\/strong>. Questo studio intende valutare il dosaggio migliore di Ixo-vec e del regime profilattico con corticosteroidi somministrati localmente, con o senza prednisone orale, per stabilire i parametri dei successivi studi di Fase III.<\/p><p>A luglio scorso, in occasione dell\u2019incontro annuale dell&#8217;<strong>American Society of Retinal Specialists <\/strong>(<strong>ASRS<\/strong>) a Stoccolma, sono stati presentati i <strong>primi dati dello studio LUNA, raccolti a 26 settimane<\/strong> dal suo inizio.<\/p><p>I dati hanno evidenziato che <strong>Ixo-vec possiede un buon profilo di sicurezza ed efficacia<\/strong>. La dose di farmaco impiegata, inferiore rispetto a quella dello studio OPTIC, ha comportato una <strong>minore infiammazione a parit\u00e0 di efficacia terapeutica<\/strong>, con il 100% dei pazienti esente da infiammazione post-trattamento o con infiammazione minima risolta con la profilassi prevista dallo studio. Il 76% dei pazienti \u00e8 rimasto indipendente dalle iniezioni intravitreali di anti-VEGF conservando un\u2019acuit\u00e0 visiva stabile e la terapia \u00e8 risultata vantaggiosa anche per i pazienti precedentemente trattati con Vabysmo.<\/p><p><strong>Ixo-vec rappresenta al momento l\u2019opzione terapeutica pi\u00f9 promettente per un cambio radicale nel trattamento dei pazienti con maculopatia essudativa<\/strong>.<\/p><p>La Adverum Biotechnologies comunicher\u00e0 tra non molto i dati dello studio LUNA a 9 e 12 mesi. Se questi confermeranno i risultati a 26 settimane, <strong>per i pazienti con maculopatia essudativa potrebbe schiudersi la reale aspettativa di un farmaco in grado di preservare la loro visione a lungo termine senza dover dipendere in modo stringente dalle iniezioni intravitreali<\/strong>.<\/p>\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-9214ece elementor-widget elementor-widget-spacer\" data-id=\"9214ece\" data-element_type=\"widget\" data-widget_type=\"spacer.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t\t\t<div class=\"elementor-spacer\">\n\t\t\t<div class=\"elementor-spacer-inner\"><\/div>\n\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t<\/section>\n\t\t\t\t<section class=\"elementor-section elementor-top-section elementor-element elementor-element-42b7a50 elementor-section-boxed elementor-section-height-default elementor-section-height-default\" data-id=\"42b7a50\" data-element_type=\"section\">\n\t\t\t\t\t\t<div class=\"elementor-container elementor-column-gap-default\">\n\t\t\t\t\t<div class=\"elementor-column elementor-col-100 elementor-top-column elementor-element elementor-element-5ca15ee\" data-id=\"5ca15ee\" data-element_type=\"column\">\n\t\t\t<div class=\"elementor-widget-wrap\">\n\t\t\t\t\t\t\t<\/div>\n\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t<\/section>\n\t\t\t\t<\/div>\n\t\t","protected":false},"excerpt":{"rendered":"<p>Trattare la maculopatia essudativa con una sola iniezione intravitreale \u00e8 l\u2019obiettivo a cui stanno lavorando da diversi anni alcuni gruppi di ricerca internazionali. Oggigiorno i pazienti affetti da maculopatia essudativa devono aderire a una terapia iniettiva a base di anti-VEGF, che prevede di iniettare direttamente all\u2019interno dell\u2019occhio, mediante iniezione intravitreale, un farmaco in grado di&#8230;<\/p>\n","protected":false},"author":13,"featured_media":13193,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"footnotes":""},"categories":[63],"tags":[],"class_list":["post-13191","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-novita","nt-post-class","","masonry-item","col-lg-4","excerpt-none"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v22.3 - https:\/\/yoast.com\/wordpress\/plugins\/seo\/ -->\n<title>Maculopatia essudativa: una terapia genica potrebbe curarla con una sola iniezione -<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/romevisionclinic.com\/it\/maculopatia-essudativa-una-terapia-genica-potrebbe-curarla-con-una-sola-iniezione\/\" \/>\n<meta property=\"og:locale\" content=\"it_IT\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"Maculopatia essudativa: una terapia genica potrebbe curarla con una sola iniezione -\" \/>\n<meta property=\"og:description\" content=\"Trattare la maculopatia essudativa con una sola iniezione intravitreale \u00e8 l\u2019obiettivo a cui stanno lavorando da diversi anni alcuni gruppi di ricerca internazionali. Oggigiorno i pazienti affetti da maculopatia essudativa devono aderire a una terapia iniettiva a base di anti-VEGF, che prevede di iniettare direttamente all\u2019interno dell\u2019occhio, mediante iniezione intravitreale, un farmaco in grado di...\" \/>\n<meta property=\"og:url\" content=\"https:\/\/romevisionclinic.com\/it\/maculopatia-essudativa-una-terapia-genica-potrebbe-curarla-con-una-sola-iniezione\/\" \/>\n<meta property=\"og:site_name\" content=\"Rome Vision Clinic\" \/>\n<meta property=\"article:published_time\" content=\"2024-10-21T08:01:32+00:00\" \/>\n<meta property=\"article:modified_time\" content=\"2024-10-21T08:07:19+00:00\" \/>\n<meta property=\"og:image\" content=\"https:\/\/romevisionclinic.com\/wp-content\/uploads\/2024\/10\/maculopatia-terapiagenica.jpg\" \/>\n\t<meta property=\"og:image:width\" content=\"724\" \/>\n\t<meta property=\"og:image:height\" content=\"483\" \/>\n\t<meta property=\"og:image:type\" content=\"image\/jpeg\" \/>\n<meta name=\"author\" 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